a-L-iduronidase gene-based therapy using phiC31 system to treat Mucopolysaccharidose type I mice

Publicado em 01/01/2015

Stilhano RS, Martin PK, de Melo SM, Samoto VY, Peres GB, Michelacci YM, da Silva FH, Pereira VG, D’Almeida V, da Cruz AT, Jasiulionis MG, Han SW